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Registration is now open for the Defeat
#Duchenne Family Forum in Montréal! Presented by@PTCbio and in partnership with@laforcedmd, join@Jesses_Journey for a day of education and inspiration on Saturday, May 2, 2020: https://bit.ly/2REMJyQ . -
Thank you to the
@JettFoundation for hosting the#ReadySetJett Family Workshop, where we joined families impacted by#Duchenne to share about our urgent mission to bring therapies to those living with#raredisease.pic.twitter.com/Y30UORy1Vh
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Interim data shows adding
#Translarna to SoC improves mobility in boys w/ nonsense mutation#DMD Codon-read-through therapy delayed disease#progression, maintained#mobility longer & preserved#pulmonary function https://doi.org/10.2217/cer-2019-0171 …#MuscularDystrophy#Duchenne#openaccesspic.twitter.com/dQ0FdcSsD7
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We are encouraged by
#realworld data from the STRIDE registry now published in@fsgcer. Making a real difference to the lives of people with#Duchenne and their families is what drives us. -
What a fantastic day for
@MDUK_News family fund Defeating#Duchenne Kerrs Cause raising an incredible £930.95 at today's@Tesco Redding#charity collection!#welldone and#thankyou to everyone who helped raise these vital#fundraising#donations#MusclesMatterpic.twitter.com/MMrzY804Xx
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Newly published MDUK-funded research by
@OxfordMedSci has increased our understanding of how the discontinued#Duchenne drug,#ezutromid works. This could help inform future research. Read more >> http://bit.ly/36SfnAU pic.twitter.com/iJAidRiVZu
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Read this systematic review of
#DMD#Duchenne https://twitter.com/christelleponsb/status/1223612287887515648 …
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Rock & Roll Saturday filling out ADHD and Autism questionnaires. Cormac doesn't need any more labels, people need to understand that
#duchenne is not just a muscle issue. Duchenne can also come with a smorgasbord of traits from sensory to Asperger. -
Congratulations to our ambassador Andy Farrell on a winning start as head coach of
@IrishRugby We can never thank Faz enough for all his support since Jack was diagnosed with#Duchenne He’s been with us on every step of this journey to find a treatment for Duchenne#SixNations -
If anybody could kindly donate it would be greatly appreciated!!!

#duchenne#musculardystrophy#donatehttps://www.justgiving.com/crowdfunding/max-taylorduchennefighter?utm_medium=email&utm_source=ExactTarget&utm_campaign=20200201_114094 … -
If you’ve ever wondered what muscle weakness looks like then this is a real life example. He brings up his knees first, followed by using his head to take some of the weight of his torso before being able to lift his arms to support himself.
#Duchenne#DMD#Disabilitypic.twitter.com/RUwO5mf8cp -
How will you be raising awareness about
#Duchenne or#Becker muscular dystrophy on@rarediseaseday? These helpful infographics add extra force to your effort
https://twitter.com/rarediseaseday/status/1223214532430061570 …
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This Helps Prevent
#Duchenne- Related Heart Disease, According to New Research https://buff.ly/2tk3Hcr#musculardystrophypic.twitter.com/SRZRZztpFW
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“Everything I do, I do it for you...”
#Duchenne#DMD#Disabilitypic.twitter.com/GFCWTMe9XL
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I’m so, so proud of the advocacy work I’ve done with [XX company] regarding accessibly... some positive changes for my local town to be announced soon.

Maybe life isn’t about fixing my child for society, but fixing society for my child. 
#Duchenne#DMD#Disability -
Who doesn't enjoy a good forward looking statement? Thanks to the
@JettFoundation for organizing an excellent Family Workshop in Worcester for boys with#Duchenne and their families pic.twitter.com/S3H6dUyJJT
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We're partnering with 18 other global organisations to study dystrophin in the brain in
#Duchenne and#Becker muscular dystrophy. Our role in the#EU_BIND project is to ensure optimal involvement and outreach to patients and their families. More → https://worldduchenne.org/bind-kickoff pic.twitter.com/Va4u7hdDGf
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A new
#genetherapy using#CrisprCas9 to excise a defective gene segment from the#DNA may provide permanent relief from#Duchenne#musculardystrophy: http://go.tum.de/307799#dmd#genomeediting -
Quantitative MRI is a better outcome measure for progression of
#Duchenne muscular dystrophy, in terms of sensitivity and reliability. 6-minute walk test, not so much... Nagy et al., 2020 https://www.ncbi.nlm.nih.gov/pubmed/31469921 pic.twitter.com/pX4UPtMpPm
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A German research team has used
#CRISPR to successfully correct the mutated gene responsible for#Duchenne#MuscularDystrophy in living pigs.https://bit.ly/38K85AF
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