Rezultati pretraživanja
  1. prije 4 sata

    Registration is now open for the Defeat Family Forum in Montréal! Presented by and in partnership with , join for a day of education and inspiration on Saturday, May 2, 2020: .

  2. prije 6 sati

    Thank you to the for hosting the Family Workshop, where we joined families impacted by to share about our urgent mission to bring therapies to those living with .

  3. prije 6 sati

    Interim data shows adding to SoC improves mobility in boys w/ nonsense mutation Codon-read-through therapy delayed disease , maintained longer & preserved function

  4. prije 7 sati

    We are encouraged by data from the STRIDE registry now published in . Making a real difference to the lives of people with and their families is what drives us.

  5. 2. velj

    What a fantastic day for family fund Defeating Kerrs Cause raising an incredible £930.95 at today's Redding collection! and to everyone who helped raise these vital

  6. Newly published MDUK-funded research by has increased our understanding of how the discontinued drug, works. This could help inform future research. Read more >>

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  7. 2. velj
  8. 1. velj

    Rock & Roll Saturday filling out ADHD and Autism questionnaires. Cormac doesn't need any more labels, people need to understand that is not just a muscle issue. Duchenne can also come with a smorgasbord of traits from sensory to Asperger.

  9. 1. velj

    Congratulations to our ambassador Andy Farrell on a winning start as head coach of We can never thank Faz enough for all his support since Jack was diagnosed with He’s been with us on every step of this journey to find a treatment for Duchenne

  10. 1. velj
  11. If you’ve ever wondered what muscle weakness looks like then this is a real life example. He brings up his knees first, followed by using his head to take some of the weight of his torso before being able to lift his arms to support himself.

  12. How will you be raising awareness about or muscular dystrophy on ? These helpful infographics add extra force to your effort 👏

  13. 30. sij

    This Helps Prevent - Related Heart Disease, According to New Research

  14. “Everything I do, I do it for you...”

  15. I’m so, so proud of the advocacy work I’ve done with [XX company] regarding accessibly... some positive changes for my local town to be announced soon. ☺️😎 Maybe life isn’t about fixing my child for society, but fixing society for my child. ❤️💪🏼

  16. 29. sij

    Who doesn't enjoy a good forward looking statement? Thanks to the for organizing an excellent Family Workshop in Worcester for boys with and their families

  17. We're partnering with 18 other global organisations to study dystrophin in the brain in and muscular dystrophy. Our role in the project is to ensure optimal involvement and outreach to patients and their families. More →

  18. 28. sij

    A new using to excise a defective gene segment from the may provide permanent relief from :

  19. 28. sij

    Quantitative MRI is a better outcome measure for progression of muscular dystrophy, in terms of sensitivity and reliability. 6-minute walk test, not so much... Nagy et al., 2020

  20. 27. sij

    A German research team has used to successfully correct the mutated gene responsible for in living pigs.

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