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A little Angelman Syndrome 101! This science teacher is nerding out on all the genetic information being shared!

#FASTSummit2019 pic.twitter.com/raPZFMR5bv
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Joe Anderson of
@UCDavisStemCell @UcdavisT presents his data showing near complete rescue of#AngelmanSyndrome deficits in adult mice at#FASTSummit2019 pic.twitter.com/wZ3jnOm6QI
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Roche/Genentech announces a clinical trial will start in 2020 of their antisense oligonucleotide (ASO/LNA)! They tested 2500 ASOs then tested the best one in monkeys, showing an increase in both UBE3A mRNA and protien. This is great news for
#AngelmanSyndrome.#FASTSummit2019 -
Ionis announces they will start a clinical trial for their ASO targeting
#AngelmanSyndrome in late 2020! Looks like 2020 will be remembered as the turning point in the fight against Angelman!#FASTSummit2019 -
trumacro is at the annual summit for FAST and our team is thrilled to talk with families of children with Angelman Syndrome. We are handing out samples of trumacro Ketogenic BHB+MCT.
@cureangelman#FastSummit2019#AngelmanSyndromepic.twitter.com/tE5tXyucSP
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Glad to be at
#FASTsummit2019 with the@OvidRx team, meeting families & learning about scientific progress in understanding & treating#AngelmanSyndrome.pic.twitter.com/5AhLpt6I61
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Thank you! Hope everyone has a wonderful weekend. I’m looking forward to checking out Chicago’s holiday decorations tonight & tomorrow afternoon while I am here for
#FASTsummit2019. -
Ionis Pharmaceuticals has announced their ASO will be headed to clinical trial in the 2nd half of 2020! We have been watching the dramatic & beneficial affect of these therapies for other disorders. Now it is our turn.
#fastSUMMIT2019#fastGALA2019#cureangelmannowpic.twitter.com/TS1eyppeE2
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At
#FastSummit2019, I announced progress in the ongoing clinical development of OV101, our investigational therapy for#Angelmansyndrome and#FragileX syndrome. (@AmitR_nyc) -
If you missed the update on Ovid’s OV101
#clinicalstudies STARS & NEPTUNE, presented last month at the@cureangelman#FASTSummit2019, by our President & Chief Medical Officer@AmitR_nyc, you can watch it online at https://www.facebook.com/cureangelman.org/videos/449416895951382/ …. -
That wraps up our
#Twitterchat! If you’d like to ask a question, reply below and we’ll try to follow-up.#Angelmansyndrome#FASTsummit2019 (@AmitR_nyc) -
*SCIENCE SUMMIT ANNOUNCEMENT* GeneTx, in partnership with Ultragenyx, Inc,. has announced that their gene altering ASO therapy will be headed to clinical trial in the FIRST half of 2020!
#fastSUMMIT2019#fastGALA2019#cureangelman#cureangelmannowpic.twitter.com/ETIgmFJt1s
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Neuren Pharmaceuticals, Inc. announces their drug NNZ-2591 will begin phase 1 trials in Australia with Phase 2 trials in the US in the second half of 2020!
#fastSUMMIT2019#fastGALA2019#FASTcantstopwontstop#cureangelman#cureangelmannow#rarechromo#genetherapy#rarediseasepic.twitter.com/IrfebEb7tA
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I am a learner! I will continue! This is for you David
#CantStopWontStop#FASTGala2019#FASTSummit2019 @ Hyatt Regency Chicago https://www.instagram.com/p/B5vOoNBneXLDW-5_osc2dpcWO3_A6y827mrM-I0/?igshid=1a977ixkrfd0b … -
Great things happening in research for potential therapies for Angelman’s Syndrome. Thanks Dr. Allyson Berent.
@cureangelman#CantStopWontStop#FASTSummit2019 pic.twitter.com/pSTiKm25kw
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Here’s Ryan Dant in 2018. The story of hope and determination for the treatment of a rare genetic disease by a father, a foundation, and a researcher. Thanks for this Emil Kakkis.
#raredisease@cureangelman#FASTSummit2019@TheRyanFndnhttps://twitter.com/TheRyanFndn/status/961425651654852608 …
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